Since this is genetic theraphy, it would be amazing if it corrected the bad roll permanently. Being in-utero, this might be the case here.
Since this is genetic theraphy, it would be amazing if it corrected the bad roll permanently. Being in-utero, this might be the case here.
Spina Bifida is not primarily a genetic disease. It's caused by a failure of the neural tube in the developing embryo to close fully. No one knows the exact causes, but folic acid deficiency in the mother before and during pregnancy makes it more likely. It also seems to run in families a little, but only weakly, and we haven't identified any specific genetic cause. This treatment is very promising, but it's not a cure, just a (hopefully) even better treatment than the existing in-utero surgery that doesn't include stem cells.